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Genzyme Corporate Pipeline

    Research     Preclinical     Phase 1     Phase 2     Phase 3     Postmarketing Studies  
  GENETIC DISEASE
Cerezyme
product enhancements

Fabrazyme
multiple studies

Genz-112638 small molecule
Gaucher disease

   
Acid sphingomyelinase
type B Niemann-Pick disease

     
Acid sphingomyelinase
type A Niemann-Pick disease

       
Myozyme
next generation

       
  RENAL DISEASE
Renvela
chronic kidney disease on dialysis

Renvela
chronic kidney disease

 
Renvela
powder formulation

 
GC1008
kidney sclerosis

   
Small molecule
polycystic kidney disease

       
Genz - 644470
hyperphosphatemia

       
  ORTHOPAEDICS AND BIOSURGICAL SPECIALTIES
Synvisc-One
osteoarthritis pain relief

Hylastan (EU)
new formulation

 
Sepraspray (EU)
new formulation adhesion barrier

 
Next generation adhesion barrier

       
Next generation osteoarthritis pain relief

       
Next generation cartilage repair
         
  ONCOLOGY
Campath
chronic lymphocytic leukemia

Clolar
pediatric acute lymphocytic leukemia

Clolar
adult acute myeloid leukemia

 
Mozobil
tumor sensitization

   
Thymoglobulin
myelodysplastic syndromes

   
Clofarabine
myelodysplastic syndromes

   
GC1008
solid tumors

     
  ENDOCRINOLOGY
TSH
nontoxic multinodular goiter

   
  TRANSPLANT AND IMMUNE DISEASE
Mozobil
stem cell mobilization

 
Alemtuzumab
multiple sclerosis

 
Thymoglobulin
living kidney donor

   
Thymoglobulin
liver transplant

   
GC1008
pulmonary fibrosis

     
Hectorol
psoriasis

     
Fc receptor antagonist
idiopathic thrombocytopenic purpura

     
  EARLY-STAGE PROMISE
Mipomersen
LDL-C reduction

 
Gene therapy
peripheral arterial disease

   
Clolar
solid tumors

     
Gene therapy
Parkinson's disease

     
Tasidotin
solid tumors

       
Topoisomerase I inhibitors
solid tumors

       
Gene therapy
age-related macular degeneration

       
Genz - 642347
type 2 diabetes

       
Genz - 29155
solid organ transplant

       
Campath
immune-mediated diseases
         

Genetics/Diagnostics Pipeline

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